Highlights from the 2025 Muscular Dystrophy Association (MDA) Conference include clinical updates, expert insights, and ...

Fakeeh University Hospital is emerging as a global destination for advanced gene therapy, delivering highly specialized ...

Italfarmaco & JCR Pharma enter commercialisation agreement for givinostat to treat Duchenne muscular dystrophy in Japan: Milan, Italy Monday, December 29, 2025, 14:00 Hrs [IST] It ...

Chennai: The Institute of Child Health (ICH) has seen a sharp rise in cases of genetic disorders since its launch in 2022, ...

Recent approval for cutting-edge gene therapy is one part of building a hub for research, collaboration and advancement ...

JCR Pharmaceuticals and Italfarmaco announced an exclusive licensing agreement for the development and commercialization of givinostat in Japan.

Get the live share price of Sarepta Therapeutics Inc (SRPT), including intraday charts, historical performance, key financials, and market updates. Track the latest US stock market activity.

The US HHS has added Duchenne muscular dystrophy and metachromatic leukodystrophy to newborn screening, citing benefits of early detection and access to FDA-approved treatments.

HHS has announced the addition of Duchenne muscular dystrophy and metachromatic leukodystrophy to the Recommended Uniform ...

Stanford Medicine researchers found that a smartphone could monitor patients with two types of muscular dystrophy as well as traditional methods and diagnose conditions more accurately - at no cost.

Consensus directed medical therapy (CDMT) was used in 73.1% of DMD patients with moderate or severe left ventricular dysfunction, leaving nearly 30% without recommended treatment. Target doses were ...