SAN DIEGO — A 9-year-old boy with Duchenne Muscular Dystrophy is enjoying recess on the playground thanks to a custom-built Formula One-style racetrack at Linda Vista Elementary School in San Diego.

People with Duchenne muscular dystrophy have a shorter-than-average life expectancy due to changes in muscles that affect breathing, heart activity, and other functions. However, treatment advances ...

MARYVILLE, Tenn. — Nine-year-old Will Leko loves Pokémon, swimming and video games. His favorite titles include Yoshi’s Crafted World and Super Mario Odyssey. But Will is also living with something ...

A gene therapy for Duchenne muscular dystrophy caused complications to the liver, prompting a review of its use for younger patients. By Christina Jewett The Food and Drug Administration said on ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

Last month we told you about a local 9-year-old boy with a challenging disease and how the community was rallying around him to help him get a van that could change his life. Well, he got that van! It ...

ST. LOUIS — The 2025 Muscular Dystrophy Association "Show of Strength" on Sunday raised more than $195,000 to help people living with neuromuscular diseases in the St. Louis area. For nearly 40 years, ...